Mom From India Shares Rare Disease Gene Therapy Clinical Trial Experience

Ms. Raja Story: https://teachrare.org/mom-from-india-shares-her-experience-with-aadc-gene-therapy/
Ms. Raja defied what others thought was impossible. She overcame all obstacles so her son, Adiroop, could have life-saving gene therapy for a rare disease known as aromatic l-amino acid decarboxylase deficiency (AADC Deficiency). Despite setbacks, Ms. Raja never gave up hope. In March 2023, Adi became the first patient in Israel to have gene therapy directly to the brain. Listen to the full story of this determined mother.